A prognostic model for predicting individual 5-year motor function trajectories in Duchenne muscular dystrophy patients using the North Star Ambulatory Assessment.

Establishes minimal detectable change thresholds for the North Star Ambulatory Assessment in Duchenne muscular dystrophy, accounting for variation across the functional spectrum.

Long-term survival analysis comparing eteplirsen-treated Duchenne muscular dystrophy patients to matched natural history controls, demonstrating survival benefits with treatment.

A framework for developing and validating multi-domain composite endpoints for AL amyloidosis clinical trials, developed through a public-private partnership with the FDA.

This study evaluates Maryland’s global budget reform in rural hospitals, finding that the reform decreased outpatient utilization but did not significantly affect inpatient admissions.

Using Health and Retirement Study data linked to occupational classifications, this study examines how lifetime job demands relate to disability in later life.

Using data from the VHA linked to Medicare claims, this study analyzed the rate to which Veterans at high risk of stroke received recommended anticoagulation therapy, finding suboptimal rates of guideline-concordant prescribing.

This protocol describes a stepped-wedge cluster randomised trial evaluating the VA Telederm mobile app for improving access to dermatology services in the Veterans Health Administration.

This study quantifies the relationship between social media use and research dissemination in plastic surgery, finding that journal audience size matters more than author social media activity.

This comparative study examines long-term care insurance systems in Korea, Japan, and Germany, drawing lessons for developing countries on financing, benefits design, and eligibility.

This article describes the development of Vermont’s single-payer health care proposal, projecting significant savings and economic benefits from the proposed reform.